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A Phase 1/2, Open-Label Study to Evaluate the Safety and Efficacy of Autologous CD19-specific Chimeric Antigen Receptor T cells (CABA-201) in Subjects with Active Idiopathic Inflammatory Myopathy or Active Juvenile Idiopathic Inflammatory Myopathy

Status
Not yet recruiting
Phases
Phase 1Phase 2
Study type
Interventional
Source
EU CTIS
Registry ID
CTIS2025-521145-24-01
Enrollment
13
Registered
2026-04-28
Start date
Unknown
Completion date
Unknown
Last updated
2026-04-30

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Active Idiopathic Inflammatory Myopathy including dermatomyositis, anti-synthetase syndrome, immune-mediated necrotizing myopathy or Juvenile Idiopathic Inflammatory Myopathy

Brief summary

Incidence and severity of AEs

Detailed description

Incidence and severity of AEs, including changes in laboratory values and vital signs, Levels of B cells in the blood, Levels of CABA-201-positive T cells in the blood, Levels of muscle enzymes (CK, LDH, AST, ALT, and aldolase) in serum, Levels of autoantibodies from the Myositis-Specific Autoantibody Panel (e.g., MDA-5, Jo-1, and HMGCR) in the serum, Total Improvement Score (0 to 100, with higher scores indicating greater improvement) based on the Core Set Measures

Interventions

DRUGFludarabin Accord 25 mg/ml Konzentrat zur Herstellung einer Injektions- /Infusionslösung
DRUGEndoxan Baxter 1 g Polvere per soluzione iniettabile
DRUGFludarabina Teva
DRUGconcentrato per soluzione iniettabile o per infusione

Sponsors

Cabaletta Bio Inc.
Lead SponsorINDUSTRY

Eligibility

Sex/Gender
All
Age
0 Years to 64 Years

Design outcomes

Primary

MeasureTime frame
Incidence and severity of AEs

Secondary

MeasureTime frame
Incidence and severity of AEs, including changes in laboratory values and vital signs, Levels of B cells in the blood, Levels of CABA-201-positive T cells in the blood, Levels of muscle enzymes (CK, LDH, AST, ALT, and aldolase) in serum, Levels of autoantibodies from the Myositis-Specific Autoantibody Panel (e.g., MDA-5, Jo-1, and HMGCR) in the serum, Total Improvement Score (0 to 100, with higher scores indicating greater improvement) based on the Core Set Measures

Outcome results

None listed

Source: EU CTIS · Data processed: May 1, 2026