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A Phase 2 Study of Cediranib in Combination With Olaparib in Advanced Solid Tumors

A Phase 2 Study of Cediranib in Combination With Olaparib in Advanced Solid Tumors

Status
Active, not recruiting
Phases
Phase 2
Study type
Interventional
Source
ClinicalTrials.gov
Registry ID
NCT02498613
Enrollment
122
Registered
2015-07-15
Start date
2016-08-31
Completion date
2026-04-10
Last updated
2025-09-25

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Advanced Malignant Solid Neoplasm, Metastatic Lung Non-Small Cell Carcinoma, Metastatic Lung Small Cell Carcinoma, Metastatic Pancreatic Adenocarcinoma, Metastatic Triple-Negative Breast Carcinoma, Pancreatic Ductal Adenocarcinoma, Stage III Breast Cancer AJCC v7, Stage III Lung Non-Small Cell Cancer AJCC v7, Stage III Lung Small Cell Carcinoma AJCC v7, Stage III Pancreatic Cancer AJCC v6 and v7, Stage IIIA Breast Cancer AJCC v7, Stage IIIA Lung Non-Small Cell Cancer AJCC v7, Stage IIIA Lung Small Cell Carcinoma AJCC v7, Stage IIIB Breast Cancer AJCC v7, Stage IIIB Lung Non-Small Cell Cancer AJCC v7, Stage IIIB Lung Small Cell Carcinoma AJCC v7, Stage IIIC Breast Cancer AJCC v7, Stage IV Breast Cancer AJCC v6 and v7, Stage IV Lung Non-Small Cell Cancer AJCC v7, Stage IV Lung Small Cell Carcinoma AJCC v7, Stage IV Pancreatic Cancer AJCC v6 and v7, Triple-Negative Breast Carcinoma, Unresectable Lung Small Cell Carcinoma, Unresectable Pancreatic Adenocarcinoma, Unresectable Pancreatic Carcinoma, Unresectable Triple-Negative Breast Carcinoma

Brief summary

This phase II trial studies cediranib maleate in combination with olaparib in treating patients with solid tumors that have spread to other parts of the body (advanced/metastatic) or cannot be removed by surgery (unresectable), including breast cancer, non-small cell lung cancer, small cell lung cancer, and pancreatic cancer. Cediranib maleate and olaparib may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth. Cediranib maleate may also block the flow of oxygen to the tumor, and may help make the tumor more sensitive to olaparib.

Detailed description

PRIMARY OBJECTIVE: I. To determine the objective response rate (ORR) of cediranib (cediranib maleate) plus olaparib in combination in patients with advanced or metastatic solid tumors of the following tumor types: non-small cell lung cancer (NSCLC), triple negative breast cancer (TNBC), pancreatic ductal adenocarcinoma (PDAC), and small cell lung cancer (SCLC). SECONDARY OBJECTIVES: I. To assess the safety and tolerability of oral administration of cediranib in combination with olaparib in patients with select advanced solid tumors. II. To estimate progression free survival (PFS) in each tumor cohort. EXPLORATORY OBJECTIVES: I. To estimate the prevalence of the mutations of deoxyribonucleic acid (DNA) repair genes in tumors using the BROCA panel and to correlate tumor regression with mutations status. (Integrated) II. To evaluate changes in tumor hypoxia on cediranib treatment compared to baseline by \[F-18\] fluoromisonidazole (FMISO) positron emission tomography/computed tomography (PET/CT) in patients with NSCLC. III. To evaluate levels of angiogenesis/inflammatory markers including VEGF at baseline and on treatment. IV. To evaluate levels of circulating tumor deoxyribonucleic acid (ctDNA) at baseline and on treatment. OUTLINE: Patients receive cediranib maleate orally (PO) once daily (QD) on day 1. Patients undergoing FMISO scan also receive olaparib PO twice daily (BID) beginning the day after the second FMISO scan and the rest of the patients receive olaparib PO BID beginning day 4 of cycle 1. Cycles repeat every 28 days (35 days for cycle 1) in the absence of disease progression or unacceptable toxicity. After completion of study treatment, patients are followed up for 4 weeks. Patients who discontinue the study treatment for reasons other than disease progression or withdrawal of consent will continue to be followed every 4 weeks until disease progression, start of new therapy, or death, whichever occurs first.

Interventions

Correlative studies

DRUGCediranib Maleate

Given PO

OTHERLaboratory Biomarker Analysis

Correlative studies

DRUGOlaparib

Given PO

PROCEDUREPositron Emission Tomography

Correlative studies

Sponsors

AstraZeneca
CollaboratorINDUSTRY
National Cancer Institute (NCI)
Lead SponsorNIH

Study design

Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT
Masking
NONE

Eligibility

Sex/Gender
ALL
Age
18 Years to No maximum
Healthy volunteers
No

Inclusion criteria

* Patients must have histologically confirmed, metastatic or unresectable malignancy of the following types: (a) non-small cell lung cancer (NSCLC), (b) triple-negative breast cancer (TNBC; defined by estrogen receptor \[ER\] \< 1%, progesterone receptor \[PR\] \< 1% and HER2 1+ or less by immunohistochemistry \[IHC\]; if HER-2 expression is 2+, a negative fluorescence in situ hybridization \[FISH\] testing is required) (c) pancreatic adenocarcinoma (PDAC), or (d) small cell lung cancer (SCLC) * Must have received at least one line of standard systemic treatment for locally advanced or metastatic disease setting of the respective tumor type; for NSCLC, it is either PD-1/PD-L1 inhibitor, or platinum-containing chemotherapy, or an EGFR tyrosine kinase inhibitor or an ALK inhibitor if sensitizing mutation present; TNBC: platinum-containing chemotherapy; PDAC: fluorouracil (5-FU-), gemcitabine-, or taxane-containing chemotherapy either with or without radiation therapy; SCLC: platinum-containing chemotherapy for limited or extensive stage disease * Patients must have measurable disease by Response Evaluation Criteria in Solid Tumors (RECIST) version (v)1.1 * Toxicities of prior therapy (except alopecia) should be resolved to =\< grade 1 as per National Cancer Institute (NCI)-Common Terminology Criteria for Adverse Events (CTCAE) version (v)5.0; patients with long-standing stable grade 2 neuropathy or prior grade 2 treatment-related hypothyroidism requiring treatment, provided free T4 within normal range, may be considered eligible after discussion with the study principal investigator (PI) * Eastern Cooperative Oncology Group (ECOG) performance status 0, 1 or 2 (Karnofsky \>= 50%) * Life expectancy of \>= 4 months * Leukocytes \>= 3,000/mcL * Absolute neutrophil count \>= 1,500/mcL * Platelets \>= 100,000/mcL * Hemoglobin \> 9 g/dL * Total bilirubin =\< 1.5 x the institutional upper limit of normal (ULN) * Aspartate aminotransferase (AST) (serum glutamic oxaloacetic transaminase \[SGOT\])/alanine aminotransferase (ALT) (serum glutamate pyruvate transaminase \[SGPT\]) =\< 2.5 x institutional ULN * Creatinine =\< 1.5 x ULN OR * Creatinine clearance \>= 45 mL/min/1.73 m\^2 for patients with creatinine levels above institutional normal; the creatinine clearance is calculated using Cockcroft-Gault formula * A urine protein: creatinine ratio of \< 1 or \< 1 g protein on 24-hour urine collection * International normalized ration (INR) within 1.25 x ULN institutional limits, except where a lupus anti-coagulant has been confirmed * Activated partial thromboplastin time (aPTT) within 1.25 x ULN institutional limits, except where a lupus anti-coagulant has been confirmed * Patients must be able to tolerate oral medications and not have gastrointestinal illnesses that would preclude absorption of cediranib or olaparib * Adequately controlled thyroid function defined by free T4 within normal range, with no symptoms of thyroid dysfunction * Adequately controlled blood pressure (BP) \< 140 mmHg (systolic) and \< 90 mmHg (diastolic) taken in the clinic setting by a medical professional within 2 weeks prior to starting study; patients with hypertension may be managed with up to a maximum of 3 antihypertensive medications; patients who are on 3 antihypertensive medications are highly recommended to be followed by a cardiologist or blood pressure specialist for management of BP while on protocol * Patients who have the following risk factors are considered to be at increased risk for cardiac toxicities, and must have documented left ventricular ejection fraction (LVEF) by echocardiogram greater than institution's lower limit of normal (or 55% if threshold for normal not otherwise specified by institutional guidelines) obtained within 3 months * Prior treatment with anthracyclines * Prior treatment with trastuzumab * A New York Heart Association (NYHA) classification of II controlled with treatment * Prior central thoracic radiation therapy (RT), including RT to the heart * History of myocardial infarction within 12 months (patients with history of myocardial infarction within 6 months are excluded from the study) * The effects of cediranib and olaparib on the developing human fetus are unknown; for this reason, women of child-bearing potential and men must agree to use adequate contraception (hormonal or barrier method of birth control; abstinence) prior to study entry and for the duration of study participation; should a woman become pregnant or suspect she is pregnant while she or her partner is participating in this study, she should inform her treating physician immediately; men treated or enrolled on this protocol must also agree to use adequate contraception prior to the study, for the duration of study participation, and for 4 months after completion of cediranib and olaparib administration * Ability to understand and the willingness to sign a written informed consent document * Age \>= 18 years. There is no dosing or adverse event data currently available on the use of cediranib or olaparib in patients \< 18 years of age, thus excluding them from enrollment

Exclusion criteria

* Patients who have had chemotherapy or RT within 3 weeks prior to start of the study agents, or those who have not recovered from adverse events due to agents administered more than 3 weeks earlier * Patients should not have received any other investigational agents within the past 4 weeks * Patients with untreated brain metastases, spinal cord compression, or evidence of symptomatic brain metastases or leptomeningeal disease as noted on computed tomography (CT) or magnetic resonance imaging (MRI) scans should be excluded from this clinical trial, since neurologic dysfunction may confound the evaluation of neurologic and other adverse events (AEs); screening brain MRI (or CT if MRI contraindicated) will be required for patients with recurrent NSCLC, TNBC, or SCLC; brain MRI (or CT if MRI contraindicated) is required for PDAC if clinically suspected by patient's symptoms or neurological exam; should patient found to have brain metastasis, treatment of brain metastasis must precede the participation in this study; for patients with known and treated brain metastases is allowed in this study if they fulfill the following criteria: * The lesions have improved or remained stable radiographically and clinically for at least 6 weeks after completion of brain irradiation or stereotactic brain radiosurgery and off steroids for at least 6 weeks * Patients who have received prior inhibitor of VEGF signaling and a poly (ADP-ribose) polymerases (PARP) inhibitor administered in combination; unless administered in combination, patients who received a prior PARP inhibitor or a prior VEGF-signaling inhibitor agent are allowed after discussing with the PI * History of allergic reactions attributed to compounds of similar chemical or biologic composition to cediranib or olaparib * Participants receiving any medications or substances that are strong inhibitors or inducers of cytochrome P450, family 3, subfamily A, polypeptide 4 (CYP3A4) are ineligible; dihydropyridine calcium-channel blockers are permitted for management of hypertension * Current use of natural herbal products or other complementary alternative medications (CAM) or folk remedies * Patients with concomitant or prior invasive malignancies within the past 3 years; subjects with treated limited stage basal cell or squamous cell carcinoma of the skin or carcinoma in situ of the breast or cervix are eligible * Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements * History of myocardial infarction within 6 months prior to registration * History of stroke or transient ischemic attack within 6 months prior to registration * NYHA classification of III or IV * Current cardiac arrhythmia requiring concurrent use of anti-arrhythmic drugs * History of hypertensive crisis or hypertensive encephalopathy within 3 years prior to registration * Clinically significant peripheral vascular disease or abdominal aortic aneurysm (\> 5 cm) or aortic dissection; if known history of abdominal aortic aneurysm with \>= 4 cm in diameter, all of the following must be met: * An ultrasound (US) within the last 6 months prior to registration will be required to document that it is =\< 5 cm * Patient must be asymptomatic from the aneurysm * Blood pressure must be well controlled as defined in this protocol * A major surgical procedure, open biopsy, or significant traumatic injury within 28 days prior to starting cediranib (percutaneous/endobronchial biopsies are allowed) * History of bowel obstruction within 1 month prior to starting study drugs * History of hemoptysis or any significant bleeding within the last 1 month prior to enrollment * Presence of cavitation of central pulmonary lesion * History of abdominal fistula, intra-abdominal abscess, or gastrointestinal perforation within the 3 months prior to enrollment * Patients may not have current dependency on intravenous (IV) hydration or total parenteral nutrition (TPN) * Patients may not have evidence of coagulopathy or bleeding diathesis; therapeutic anticoagulation for prior thromboembolic events is permitted; the clinical indication for therapeutic anticoagulation must be clearly documented prior to enrollment and must be discussed with the P.I.; given the increases risk of serious bleeding from cediranib, patients who are on greater than or equal to 2 anti-thrombotic agents, including but not limited to anti-platelet agents (non-steroidal anti-inflammatory drugs \[NSAIDs\]/aspirin, clopidogrel), heparin, low molecular weight heparin (LMWH), warfarin, and a direct thrombin inhibitor, will be excluded * Patients may not have features suggestive of myelodysplastic syndrome (MDS) or acute myelogenous leukemia (AML) on peripheral blood smear or bone marrow biopsy, if clinically indicated * Pregnant women are excluded from this study because olaparib and cediranib have the potential for teratogenic or abortifacient effects; due to the fact that there is an unknown but potential risk for adverse events in nursing infants secondary to treatment of the mother with olaparib and cediranib, breastfeeding should be discontinued if the mother is treated with cediranib and olaparib * Human immunodeficiency virus (HIV)-positive patients on combination antiretroviral therapy are ineligible because of the potential for pharmacokinetic interactions with cediranib or olaparib; appropriate studies will be undertaken in patients receiving combination antiretroviral therapy when indicated; HIV-positive patients with undetectable viral loads and CD4 counts \> 300, and not on any antiretroviral therapy may be allowed after discussing with the principle investigator * Any condition that, in the opinion of the treating investigator would interfere with evaluation of the investigational product or interpretation of subject safety or study results

Design outcomes

Primary

MeasureTime frameDescription
Objective Response RateUp to 4 weeks after completion of study treatment (Up to 43 months)Measured by Response Evaluation Criteria in Solid Tumors version 1.1. The exact two-sided 95% confidence interval for the objective response rate will be reported.

Secondary

MeasureTime frameDescription
Incidence of Adverse EventsUp to 4 weeks after completion of study treatment (Up to 44 months)Graded according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0. The outcome was updated upon results entry to reflect the number of graded adverse events per cohort separated by Grade 3 and Grade 4.
Progression-free SurvivalUp to 4 weeks after completion of study treatment (Up to 44 months)This outcome was updated at the time of results entry to include the median PFS and the full range of survival time in months for each cohort. The time frame was updated as well. PFS was calculated as the duration of time from start of treatment to time of progression or death, whichever occurs first, assessed up to 4 weeks after completion of study treatment.

Other

MeasureTime frameDescription
Prevalence of the Mutations of Deoxyribonucleic Acid (DNA) Repair Genes in Each Tumor CohortUp to 2 yearsIn the first 20 endpoint-evaluable patients with non-small cell lung cancer and 20 endpoint-evaluable patients with triple negative breast cancer, the exploratory analyses will be done using Fisher's exact tests, Mann-Whitney U tests or McNemar's test depending on the type of data observed.
Changes in Levels of Angiogenesis/ Inflammatory Markers (Angiome Panel) (All Cohorts)Baseline to post-therapyWill be assessed using paired t- test or Wilcoxon signed-rank.
Changes in Tumor Hypoxia by ImagingBaseline to post-cediranib monotherapyMeasured by 18F-fluoromisonidazole positron emission tomography/computed tomography scans (non-small cell lung cancer). For the pre- and post-cediranib therapy outcome analysis, paired t- test or Wilcoxon signed-rank test will be applied for the continuous variables.
Changes in Level of Circulating Tumor Deoxyribonucleic Acid (ctDNA) (All Cohorts)Baseline to post therapyWill be assessed using paired t- test or Wilcoxon signed-rank.

Countries

Canada, United States

Participant flow

Participants by arm

ArmCount
NSCLC Cohort
Non-Small Cell Lung Cancer (NSCLC) participant cohort.
31
TNBC Cohort
Triple-Negative Breast Cancer (TNBC) participant cohort.
39
PDAC Cohort
Pancreatic Ductal Adenocarcinoma (PDAC) participant cohort.
24
SCLC Cohort
Small Cell Lung Cancer (SCLC) participant cohort.
28
Total122

Withdrawals & dropouts

PeriodReasonFG000FG001FG002FG003
Overall StudyTx Initiation Criteria Not Met2151
Overall StudyWithdrawal by Subject3100

Baseline characteristics

CharacteristicTotalPDAC CohortSCLC CohortTNBC CohortNSCLC Cohort
Age, Continuous59.6 years
STANDARD_DEVIATION 10.9
64.2 years
STANDARD_DEVIATION 10.9
63.2 years
STANDARD_DEVIATION 9
50.1 years
STANDARD_DEVIATION 8.2
64.6 years
STANDARD_DEVIATION 7.8
Eastern Cooperative Oncology Group (ECOG)
0
28 Participants7 Participants5 Participants9 Participants7 Participants
Eastern Cooperative Oncology Group (ECOG)
1
87 Participants15 Participants23 Participants29 Participants20 Participants
Eastern Cooperative Oncology Group (ECOG)
2
7 Participants2 Participants0 Participants1 Participants4 Participants
Eastern Cooperative Oncology Group (ECOG)
3
0 Participants0 Participants0 Participants0 Participants0 Participants
Eastern Cooperative Oncology Group (ECOG)
4
0 Participants0 Participants0 Participants0 Participants0 Participants
Eastern Cooperative Oncology Group (ECOG)
5
0 Participants0 Participants0 Participants0 Participants0 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants1 Participants1 Participants1 Participants0 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
115 Participants23 Participants26 Participants35 Participants31 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
4 Participants0 Participants1 Participants3 Participants0 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants0 Participants0 Participants0 Participants0 Participants
Race (NIH/OMB)
Asian
0 Participants0 Participants0 Participants0 Participants0 Participants
Race (NIH/OMB)
Black or African American
0 Participants0 Participants0 Participants0 Participants0 Participants
Race (NIH/OMB)
More than one race
0 Participants0 Participants0 Participants0 Participants0 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants0 Participants0 Participants0 Participants0 Participants
Race (NIH/OMB)
Unknown or Not Reported
32 Participants5 Participants4 Participants16 Participants7 Participants
Race (NIH/OMB)
White
90 Participants19 Participants24 Participants23 Participants24 Participants
Region of Enrollment
Canada
12 participants0 participants1 participants10 participants1 participants
Region of Enrollment
United States
110 participants24 participants27 participants29 participants30 participants
Sex: Female, Male
Female
77 Participants10 Participants14 Participants39 Participants14 Participants
Sex: Female, Male
Male
45 Participants14 Participants14 Participants0 Participants17 Participants

Adverse events

Event typeEG000
affected / at risk
EG001
affected / at risk
EG002
affected / at risk
EG003
affected / at risk
deaths
Total, all-cause mortality
4 / 291 / 387 / 191 / 27
other
Total, other adverse events
29 / 2938 / 3819 / 1927 / 27
serious
Total, serious adverse events
13 / 2919 / 3812 / 1910 / 27

Outcome results

Primary

Objective Response Rate

Measured by Response Evaluation Criteria in Solid Tumors version 1.1. The exact two-sided 95% confidence interval for the objective response rate will be reported.

Time frame: Up to 4 weeks after completion of study treatment (Up to 43 months)

Population: Those analyzed for clinical activity.

ArmMeasureValue (NUMBER)
NSCLC CohortObjective Response Rate0.08 proportion of participants
TNBC CohortObjective Response Rate0.16 proportion of participants
SCLC CohortObjective Response Rate0.26 proportion of participants
PDAC CohortObjective Response Rate0 proportion of participants
Secondary

Incidence of Adverse Events

Graded according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0. The outcome was updated upon results entry to reflect the number of graded adverse events per cohort separated by Grade 3 and Grade 4.

Time frame: Up to 4 weeks after completion of study treatment (Up to 44 months)

Population: All graded adverse events (serious and non serious).

ArmMeasureGroupValue (NUMBER)
NSCLC CohortIncidence of Adverse EventsGrade 360 Adverse Events
NSCLC CohortIncidence of Adverse EventsGrade 42 Adverse Events
TNBC CohortIncidence of Adverse EventsGrade 41 Adverse Events
TNBC CohortIncidence of Adverse EventsGrade 371 Adverse Events
SCLC CohortIncidence of Adverse EventsGrade 337 Adverse Events
SCLC CohortIncidence of Adverse EventsGrade 42 Adverse Events
PDAC CohortIncidence of Adverse EventsGrade 361 Adverse Events
PDAC CohortIncidence of Adverse EventsGrade 47 Adverse Events
Secondary

Progression-free Survival

This outcome was updated at the time of results entry to include the median PFS and the full range of survival time in months for each cohort. The time frame was updated as well. PFS was calculated as the duration of time from start of treatment to time of progression or death, whichever occurs first, assessed up to 4 weeks after completion of study treatment.

Time frame: Up to 4 weeks after completion of study treatment (Up to 44 months)

Population: Those with evaluable responses.

ArmMeasureValue (MEDIAN)
NSCLC CohortProgression-free Survival3.8 months
TNBC CohortProgression-free Survival3.4 months
SCLC CohortProgression-free Survival1.8 months
PDAC CohortProgression-free Survival4.0 months
Other Pre-specified

Changes in Level of Circulating Tumor Deoxyribonucleic Acid (ctDNA) (All Cohorts)

Will be assessed using paired t- test or Wilcoxon signed-rank.

Time frame: Baseline to post therapy

Other Pre-specified

Changes in Levels of Angiogenesis/ Inflammatory Markers (Angiome Panel) (All Cohorts)

Will be assessed using paired t- test or Wilcoxon signed-rank.

Time frame: Baseline to post-therapy

Other Pre-specified

Changes in Tumor Hypoxia by Imaging

Measured by 18F-fluoromisonidazole positron emission tomography/computed tomography scans (non-small cell lung cancer). For the pre- and post-cediranib therapy outcome analysis, paired t- test or Wilcoxon signed-rank test will be applied for the continuous variables.

Time frame: Baseline to post-cediranib monotherapy

Other Pre-specified

Prevalence of the Mutations of Deoxyribonucleic Acid (DNA) Repair Genes in Each Tumor Cohort

In the first 20 endpoint-evaluable patients with non-small cell lung cancer and 20 endpoint-evaluable patients with triple negative breast cancer, the exploratory analyses will be done using Fisher's exact tests, Mann-Whitney U tests or McNemar's test depending on the type of data observed.

Time frame: Up to 2 years

Source: ClinicalTrials.gov · Data processed: Feb 18, 2026