Ataxia Telangiectasia
Conditions
Brief summary
The primary endpoint for the study is of the Scale for the Assessment and Rating of Ataxia
Detailed description
Spinocerebellar Ataxia Functional Index (SCAFI) is one of the four secondary endpoints., International Cooperative Rating Scale (ICARS) is one of the four secondary endpoints., Quality of Life EQ-5D-5L for patients aged ≥18; EQ-5D-Y for patients aged <18 years is one of the four secondary endpoints., Investigator’s, Caregiver’s (if applicable), and Patient’s (if able) Clinical Global Impression of Improvement (CGI-I) comparing end of period I (Visit 4) to baseline (Visit 2) is one of the four secondary endpoints.
Interventions
Sponsors
Intrabio Limited
Eligibility
Sex/Gender
All
Age
0 Years to No maximum
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| The primary endpoint for the study is of the Scale for the Assessment and Rating of Ataxia | — |
Secondary
| Measure | Time frame |
|---|---|
| Spinocerebellar Ataxia Functional Index (SCAFI) is one of the four secondary endpoints., International Cooperative Rating Scale (ICARS) is one of the four secondary endpoints., Quality of Life EQ-5D-5L for patients aged ≥18; EQ-5D-Y for patients aged <18 years is one of the four secondary endpoints., Investigator’s, Caregiver’s (if applicable), and Patient’s (if able) Clinical Global Impression of Improvement (CGI-I) comparing end of period I (Visit 4) to baseline (Visit 2) is one of the four secondary endpoints. | — |
Countries
Germany, Slovakia, Spain
Outcome results
None listed