N-Acetyl-L-Leucine
Sponsors
Intrabio Limited, Intrabio Limited, IntraBio Inc, IntraBio Inc
Conditions
Ataxia TelangiectasiaAtaxia-TelangiectasiaAtaxia-Telangiectasia (A-T)CACNA1ACACNA1A DisordersEpisodic Ataxia Type 2Familial Hemiplegic Migraine-1Niemann-Pick Disease, Type C
Phase 3
A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C
RecruitingNCT05163288
Start: 2022-06-30End: 2030-12-01Target: 53Updated: 2026-04-03
Effects of N-Acetyl-L-Leucine on Niemann-Pick disease type C (NPC): A Phase III, randomized, placebo-controlled, double-blind, crossover study
RecruitingCTIS2023-510278-14-00
Start: 2022-06-16Target: 60Updated: 2025-11-27
A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T)
Active, not recruitingNCT06673056
Start: 2025-03-18End: 2028-06-01Target: 60Updated: 2025-07-03
Effects of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T): A Phase III, randomized, placebo-controlled, double-blind, crossover study
RecruitingCTIS2024-517706-29-00
Start: 2025-05-13Target: 45Updated: 2025-12-01
Pivotal Study of N-acetyl-L-leucine for CACNA1A
Not yet recruitingNCT07221292
Start: 2026-09-01End: 2028-11-01Target: 60Updated: 2026-03-27
IB1001-304: Effects of N-Acetyl-L-Leucine on CACNA1A Disorders: A Phase III, randomized, placebo-controlled, double-blind, crossover study
Not yet recruitingCTIS2025-523828-51-00
Target: 10Updated: 2026-03-25