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A Phase 3 Global, Double-Blind, Randomized, Placebo-Controlled Study to Evaluate the Efficacy and Safety of ION-682884 in Patients with Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)

Status
Active, not recruiting
Phases
Phase 3
Study type
Interventional
Source
EU CTIS
Registry ID
CTIS2024-514434-20-00
Acronym
ION-682884-CS2
Enrollment
413
Registered
2024-09-17
Start date
2020-06-29
Completion date
Unknown
Last updated
2025-11-05

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)

Brief summary

Composite endpoint of CV-death and recurrent CV clinical events comparing the 2 study arms up to Week 140. Cardiovascular clinical events include: 1. Hospitalization for myocardial infarction (MI), Hospitalization for HF, Hospitalization for arrhythmia, Hospitalization for stroke/Transient Ischemic Attack TIA, HF urgent visits to ED/ER or HF clinics requiring administration of intravenous (IV) diuretics for improvement.

Interventions

DRUGPlacebo injection
DRUG0.8 ml (is a sterile
DRUGparenteral solution of sodium chloride and riboflavin in Water for Injection) for subcutaneous administration

Sponsors

Ionis Pharmaceuticals Inc.
Lead SponsorINDUSTRY

Eligibility

Sex/Gender
All
Age
18 Years to No maximum

Design outcomes

Primary

MeasureTime frame
Composite endpoint of CV-death and recurrent CV clinical events comparing the 2 study arms up to Week 140. Cardiovascular clinical events include: 1. Hospitalization for myocardial infarction (MI), Hospitalization for HF, Hospitalization for arrhythmia, Hospitalization for stroke/Transient Ischemic Attack TIA, HF urgent visits to ED/ER or HF clinics requiring administration of intravenous (IV) diuretics for improvement.

Countries

Austria, Belgium, Czechia, Denmark, France, Germany, Greece, Italy, Poland, Portugal, Spain, Sweden

Outcome results

None listed

Source: EU CTIS · Data processed: Feb 4, 2026