ION 682884
Sponsors
Ionis Pharmaceuticals Inc., Brigham and Women's Hospital
Conditions
Hereditary Transthyretin-Mediated Amyloid PolyneuropathyTransthyretin Amyloid CardiopathyTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)
Phase 2
Phase 3
An Open-Label Extension Study to Assess the Long-Term Safety of Eplontersen (ION-682884) in Patients with Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)
RecruitingCTIS2022-502415-11-00
Start: 2023-06-16Target: 339Updated: 2025-10-30
An Open-label, Extension Study to Assess the Long-Term Safety and Efficacy of ION-682884 in Patients with Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
RecruitingCTIS2024-511201-32-00
Start: 2022-06-13Target: 47Updated: 2025-11-20
A Phase 3 Global, Double-Blind, Randomized, Placebo-Controlled Study to Evaluate the Efficacy and Safety of ION-682884 in Patients with Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)
Active, not recruitingCTIS2024-514434-20-00
Start: 2020-06-29Target: 413Updated: 2025-11-05