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rAAV1-CB-hAAT
BIOLOGICAL
2 trials
Sponsors
University of Massachusetts, Worcester
, Beacon Therapeutics
Conditions
Alpha 1-Antitrypsin Deficiency
Alpha-1 Antitrypsin Deficiency
Phase 1
Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin (AAT) Deficiency
Completed
NCT00430768
University of Massachusetts, Worcester
Alpha 1-Antitrypsin Deficiency
Start: 2006-02-28
End: 2015-01-31
Updated: 2016-12-15
Phase 2
Safety & Efficacy Study of rAAV1-CB-hAAT for Alpha-1 Antitrypsin Deficiency
Completed
NCT01054339
Beacon Therapeutics
Alpha-1 Antitrypsin Deficiency
Start: 2010-06-30
End: 2015-10-31
Updated: 2019-03-28