Normal Saline as Placebo
Sponsors
Soul, Janet , M.D., Intellia Therapeutics, Onwukwe Emeka
Conditions
Amyloid NeuropathiesAmyloid Neuropathies, FamilialAmyloidosisAmyloidosis, FamilialAmyloidosis, HereditaryGenetic Disease, InbornMetabolic DiseasesMetabolism, Inborn Errors