NNZ-2591
Sponsors
Neuren Pharmaceuticals Limited
Conditions
Angelman SyndromeHealthy VolunteersPhelan-McDermid SyndromePitt Hopkins SyndromePrader-Willi Syndrome
Phase 1
Phase 2
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
CompletedNCT05011851
Start: 2022-07-12End: 2024-07-16Updated: 2025-01-31
An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)
CompletedNCT05025241
Start: 2022-08-08End: 2023-11-17Updated: 2025-06-03
An Open-Label Study of Oral NNZ-2591 in Pitt Hopkins Syndrome (PTHS-001)
CompletedNCT05025332
Start: 2022-10-14End: 2024-05-03Updated: 2025-06-18
An Open-Label Study of Oral NNZ-2591 in Prader-Willi Syndrome (PWS-001)
WithdrawnNCT05879614
Start: 2023-09-01End: 2025-06-30Updated: 2024-12-09
Phase 3
A Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid Syndrome
RecruitingNCT07281079
Start: 2025-11-12End: 2027-11-15Target: 160Updated: 2026-08-25
An Open-label Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid Syndrome
RecruitingNCT07593391
Start: 2026-06-08End: 2028-11-12Target: 180Updated: 2026-08-12