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Outcome of treatment with Triheptanoin in pediatric patients with long chain fatty acid oxidation disorders (LCFAODs)

Outcome of treatment with Triheptanoin in pediatric patients with long chain fatty acid oxidation disorders (LCFAODs) at Queen Sirikit National Institute of Child Health.

Status
Active, not recruiting
Phases
Unknown
Study type
Observational
Source
TCTR
Registry ID
TCTR20210604002
Enrollment
2
Registered
2021-06-04
Start date
2021-06-30
Completion date
Unknown
Last updated
2026-08-03

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

long chain fatty acid oxidation disorders (LCFAODs) long chain fatty acid oxidation disorders (LCFAODs), outcome, treatment

Interventions

patient with long chain fatty acid oxidation disorders (LCFAODs)
Treatment
patient

Sponsors

None listed

Eligibility

Sex/Gender
All
Age
2 Weeks to 15 Years

Inclusion criteria

Inclusion criteria: Patient with diagnosis of long chain fatty acid oxidation disorders (LCFAODs)

Exclusion criteria

Exclusion criteria: can not continue treatment until the end of research

Design outcomes

Primary

MeasureTime frame
frequency of hospitalization with rhabdomyolysis 2 years number

Secondary

MeasureTime frame
abnormality of the cardiac muscles 2 years echo

Countries

Thailand

Contacts

Public ContactDuenchai khata

Queen Sirikit National Institute of Child Health

dueanchai_khata@hotmail.com0891599650

Outcome results

None listed

Source: TCTR (via WHO ICTRP) · Data processed: Aug 9, 2026