Propionic acidemia
Conditions
Interventions
Sponsors
Danone Nutricia Research
Eligibility
Age
2 Years to 64 Years
Inclusion criteria
Inclusion criteria: Having PA (or having a sibling with PA) and age >4 yr and preferably <10 yr (upper age limit is 18 yr).
Exclusion criteria
Exclusion criteria: PA patients with confounding intestinal diseases (e.g. colon rectal cancers, Crohn's disease, Ulcerative colitis).
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| Phylogenetic composition of the gut microbiota in PA patients | — |
Contacts
Public ContactCyril Marsaux
Nutrica
Outcome results
None listed