DMD Voice: Qualitative Interviews With Patients and Caregivers

Duchenne Muscular Dystrophy Quality of Life: Qualitative Interviews With Patients and Caregivers

Status

Recruiting

Phases

Unknown

Study type

Observational

Source

ClinicalTrials.gov

Registry ID

NCT06925269

Enrollment

Registered

2025-04-13

Start date

2025-03-31

Completion date

2026-12-31

Last updated

2025-04-30

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Duchenne Muscular Dystrophy (DMD)

Keywords

Duchenne, givinostat

Brief summary

The purpose of this study is to understand DMD functional losses or abilities and their association with independence and quality of life from the perspective of individuals with DMD and/or and their caregivers. This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.

Interventions

None listed

Study design

Observational model

COHORT

Time perspective

RETROSPECTIVE

Eligibility

Sex/Gender

MALE

Age

10 Years to No maximum

Healthy volunteers

Inclusion criteria

Subsample A - Patients Eligible participants for Subsample A must: * Have been treated with Givinostat for at least 2 years * Be at least 10 years of age with signed consent of a parent or legal guardian * Be currently taking givinostat * Willing and able to participate in a video and/or audio recorded interview Subsample A - Caregivers Eligible caregivers for Subsample A must: * Be a parent or legal guardian of an individual with DMD that has been taking givinostat for at least two years * Willing and able to participate in a video and/or audio recorded interview Subsample B - Caregivers Eligible caregivers for Subsample B must: * Provide care to an individual with DMD who is unable to raise their hands above their head as confirmed by the caregiver * Reside in the United States or Canada * Able to read, speak, and understand English * Willing and able to participate in a video and/or audio recorded interview Have access to a stable internet connection

Exclusion criteria

Design outcomes

Primary

Measure	Time frame	Description
Qualitative Interview	60 minutes	Participants will participate in a semi-structured interview

Countries

United States

Contacts

Primary ContactMary Hubbard

mhubbard@rednucleus.com904-541-9326

Outcome results