Mitochondrial Neurogastrointestinal Encephalomyopathy
Conditions
Keywords
MNGIE
Brief summary
Non-interventional, prospective, multicenter, natural history study of patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)
Interventions
OTHERNon-interventional
Non-interventional natural history study
Sponsors
Entrada Therapeutics, Inc.
Study design
Observational model
COHORT
Time perspective
PROSPECTIVE
Eligibility
Sex/Gender
ALL
Age
5 Years to No maximum
Healthy volunteers
No
Inclusion criteria
* Has MNGIE
Exclusion criteria
* Substance abuser
Design outcomes
Primary
| Measure | Time frame | Description |
|---|---|---|
| MNGIE Clinical Course | 5 years | To evaluate the clinical course of MNGIE patients |
Countries
Turkey (Türkiye), United States
Outcome results
None listed