A Long-term Study for the Outcome of Pompe Disease

Status

Recruiting

Phases

Unknown

Study type

Observational

Source

ClinicalTrials.gov

Registry ID

NCT02399748

Enrollment

Registered

2015-03-26

Start date

2007-04-30

Completion date

2026-12-31

Last updated

2017-07-18

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Pompe Disease

Brief summary

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

Interventions

None listed

Study design

Observational model

CASE_ONLY

Time perspective

PROSPECTIVE

Eligibility

Sex/Gender

ALL

Healthy volunteers

Inclusion criteria

Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy

Exclusion criteria

Design outcomes

Primary

Measure	Time frame
all cause morbidities	10 years

Countries

Taiwan

Contacts

Primary ContactYin-Hsiu Chien

chienyh@ntu.edu.tw+886223123456

Outcome results