Skip to content

Etoposide, Filgrastim, and Plerixafor in Improving Stem Cell Mobilization in Treating Patients With Non-Hodgkin Lymphoma

A Study of Hematopoietic Stem Cell Supermobilization in Patients With Non-Hodgkin Lymphoma

Status
Terminated
Phases
NA
Study type
Interventional
Source
ClinicalTrials.gov
Registry ID
NCT01408043
Enrollment
25
Registered
2011-08-03
Start date
2011-10-31
Completion date
2016-05-31
Last updated
2019-06-14

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Adult Acute Lymphoblastic Leukemia in Remission, Adult Grade III Lymphomatoid Granulomatosis, Adult Nasal Type Extranodal NK/T-cell Lymphoma, Anaplastic Large Cell Lymphoma, Angioimmunoblastic T-cell Lymphoma, Cutaneous B-cell Non-Hodgkin Lymphoma, Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue, Hepatosplenic T-cell Lymphoma, Nodal Marginal Zone B-cell Lymphoma, Noncutaneous Extranodal Lymphoma, Peripheral T-cell Lymphoma, Recurrent Adult Burkitt Lymphoma, Recurrent Adult Diffuse Large Cell Lymphoma, Recurrent Adult Diffuse Mixed Cell Lymphoma, Recurrent Adult Diffuse Small Cleaved Cell Lymphoma, Recurrent Adult Grade III Lymphomatoid Granulomatosis, Recurrent Adult Immunoblastic Large Cell Lymphoma, Recurrent Adult Lymphoblastic Lymphoma, Recurrent Adult T-cell Leukemia/Lymphoma, Recurrent Cutaneous T-cell Non-Hodgkin Lymphoma, Recurrent Grade 1 Follicular Lymphoma, Recurrent Grade 2 Follicular Lymphoma, Recurrent Grade 3 Follicular Lymphoma, Recurrent Mantle Cell Lymphoma, Recurrent Marginal Zone Lymphoma, Recurrent Mycosis Fungoides/Sezary Syndrome, Recurrent Small Lymphocytic Lymphoma, Refractory Chronic Lymphocytic Leukemia, Refractory Hairy Cell Leukemia, Small Intestine Lymphoma, Splenic Marginal Zone Lymphoma, T-cell Large Granular Lymphocyte Leukemia, Testicular Lymphoma, Waldenström Macroglobulinemia

Brief summary

This clinical trial studies etoposide, filgrastim and plerixafor in improving stem cell mobilization in patients with non-Hodgkin lymphoma. Giving colony-stimulating factors, such as filgrastim, and plerixafor and etoposide together helps stem cells move from the patient's bone marrow to the blood so they can be collected and stored.

Detailed description

PRIMARY OBJECTIVES: I. To determine whether the addition of plerixafor improves the proportion of patients with lymphoma who collect \>= 8 x 10\^6 cluster of differentiation (CD)34+ cells/kg within two days by 25% compared to the historical estimate of 42% with etoposide and G-CSF (filgrastim). II. To determine whether patients achieving collection of \>= 8 x 10\^6 CD34+ cells/kg have a 15% one year survival advantage relative to the historical estimate of 68% among patients mobilizing \>= 2 but \< 8 x 10\^6 CD34+ cells/kg with etoposide and G-CSF. SECONDARY OBJECTIVES: I. To demonstrate that patients receiving \>= 8 x 10\^6 CD34+ cells/kg have more rapid neutrophil and platelet recovery and earlier hospital discharge than those receiving \< 8 x 10\^6 CD 34+ cells/kg. II. To compare overall survival and progression-free survival between patients receiving \>= 8 x 10\^6 CD34+ cells/kg and those receiving \< 8 x 10\^6 CD34+ cells/kg. III. To compare number of days of apheresis required to achieve goal, transfusion requirements, hospitalization costs, need for remobilization between groups. IV. To evaluate whether peripheral CD34+ cell count correlates with graft content of CD34+ cells. OUTLINE: Patients receive etoposide intravenously (IV) over 4 hours on day 0, filgrastim subcutaneously (SC) once daily (QD) beginning day 1, and plerixafor SC 15-18 hours prior to apheresis. Patients unable to achieve target collection of \>= 8 x 10\^6 CD34+ cells/kg receive another dose of plerixafor followed by apheresis. Following the second apheresis, patients achieving =\< 2 x 10\^6 CD34+ cells/kg may continue filgrastim with plerixafor and continue collection according to the attending physician. After completion of study treatment, patients are followed up at 28 days and then for at least 1 year.

Interventions

DRUGplerixafor

Given SC

BIOLOGICALfilgrastim

Given SC

DRUGetoposide

Given IV

PROCEDUREleukapheresis

Undergo apheresis

Sponsors

National Cancer Institute (NCI)
CollaboratorNIH
Case Comprehensive Cancer Center
Lead SponsorOTHER

Study design

Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT
Masking
NONE

Eligibility

Sex/Gender
ALL
Age
18 Years to 78 Years
Healthy volunteers
No

Inclusion criteria

* Have biopsy-confirmed non-Hodgkin lymphoma, of any type * Must be eligible for autologous transplantation according to institutional guidelines * Eastern Cooperative Oncology Group performance status of 0 or 1 * Karnofsky performance status of 70 to 100 * Negative for human immunodeficiency virus (HIV) * prior to the start of mobilization, subjects must have: * Absolute neutrophil count of \>= 1.2 x 10\^9/L * Platelet count of \>= 100 x 10\^9/L * Creatinine clearance \>= 30 mL/minute * All patients must be able to comprehend and sign informed consent * If childbearing potential must either agree to complete abstinence from heterosexual intercourse or effective means of contraception during stem cell mobilization and for at least 3 months following last plerixafor dose; female patients will undergo pregnancy test prior to stem cell mobilization therapy

Exclusion criteria

* Have had previous transplants and/or prior mobilization attempts * Have evidence of progressive non-Hodgkin lymphoma * Have evidence of bone marrow involvement of lymphoma at time of transplant staging * Had evidence of active central nervous system (CNS) involvement * Have had previous radiation of the pelvic area * Have had prior radioimmunotherapy * Have received experimental therapy within 2 weeks of enrollment * Be currently enrolled in another investigational protocol * Have prior history of other malignancies, excluding basal cell carcinoma or squamous cell carcinoma of the skin

Design outcomes

Primary

MeasureTime frameDescription
Collection Using Plerixafor, Etoposide, and FilgrastimWithin 2 days of apheresisNumber of participants able to collect equal to or more than 8 x 10\^6 CD34+ cells/kg with addition of plerixafor to etoposide and filgrastim. These participants are defined as supermobilizers. Participants with less than 8 x 10\^6 CD34+ cells/kg are defined as normal mobilizers.
Progression-free SurvivalUp to 1 year post-transplantThe number of participants of patients who receive greater than or equal to 8 x 10\^6 CD34+ cells/kg following collection with plerixafor, etoposide, and filgrastim and that have progression-free survival at one year
Overall SurvivalUp to 1 year post-transplantNumber of participants who receive greater than or equal to 8 x 10\^6 CD34+ cells/kg by 15% following collection with plerixafor, etoposide, and filgrastimstill alive at 1 yr post transplant

Secondary

MeasureTime frameDescription
Progression-free Survival in Supermobilizers and Normal MobilizersUp to 1 year post-transplantPercentage of participants who were alive and free of progression 1 year after transplant (PFS)
Overall Survival in Supermobilizers and Normal MobilizersUp to 1 year post-transplantPercentage of participants who were alive 1 year after transplant (OS)
Number of Days of Apheresis RequiredUp to 28 days post treatmentNumber of days of apheresis required to achieve goal in supermobilizers and normal mobilizers
Neutrophil Recovery in Super Mobilizers and Normal MobilizersUp to 28 days post treatmentNeutrophil recovery in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg entered as the mean cell count of super mobilizers and normal mobilizers.
Need for RemobilizationUp to 28 days post treatmentNumber of participants that needed remobilization in supermobilizers and normal mobilizers. Remobilization can be described as follows: The first step for patients undergoing autologous hematopoietic cell transplantation is to mobilize hematopoietic progenitor/stem cells from the bone marrow using G-CSF, plerixafor and/or chemotherapy. This is followed by collection of the cells by apheresis. If sufficient number of progenitor/stem cells cannot be mobilized and then collected by apheresis to proceed with transplantation, it is considered as mobilization failure. For these patients, mobilization of their hematopoietic progenitor/stem cells is attempted a second time (remobilization). The need to do a second 'mobilization' attempt is not ideal.
Correlation of Peripheral CD34+ Cell Count With Graft Content of CD34+ CellsUp to 28 days post treatmentCorrelation of peripheral CD34+ cell count with graft content of CD34+ cells assessed using Spearman correlation.
Number of Transfusion RequirementsUp to 28 days post treatmentNumber of transfusions (number of packed red blood cells and platelet transfusions required from day 0 to +28 post-transplant) in supermobilizers and normal mobilizers
Platelet Recovery in Super Mobilizers and Normal MobilizersUp to 28 days post treatmentPlatelet recovery in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg.
Length of Hospital Stay in Super Mobilizers and Normal MobilizersUp to 28 days post treatmentLength of hospital stay in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg.

Countries

United States

Participant flow

Participants by arm

ArmCount
Treatment (Stem Cell Supermobilization)
Patients receive etoposide IV over 4 hours on day 0, filgrastim SC QD beginning day 1, and plerixafor SC 15-18 hours prior to apheresis. Patients unable to achieve target collection of \>= 8 x 10\^6 CD34+ cells/kg receive another dose of plerixafor followed by apheresis. Following the second apheresis, patients achieving =\< 2 x 10\^6 CD34+ cells/kg may continue filgrastim with plerixafor and continue collection according to the attending physician. plerixafor: Given SC filgrastim: Given SC etoposide: Given IV leukapheresis: Undergo apheresis
25
Total25

Withdrawals & dropouts

PeriodReasonFG000
Overall Studyunable to collect cells1

Baseline characteristics

CharacteristicTreatment (Stem Cell Supermobilization)
Age, Continuous62.48 years
STANDARD_DEVIATION 11.14
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
25 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
Race (NIH/OMB)
Asian
0 Participants
Race (NIH/OMB)
Black or African American
2 Participants
Race (NIH/OMB)
More than one race
0 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
Race (NIH/OMB)
White
23 Participants
Region of Enrollment
United States
25 participants
Sex: Female, Male
Female
4 Participants
Sex: Female, Male
Male
21 Participants

Adverse events

Event typeEG000
affected / at risk
deaths
Total, all-cause mortality
0 / 25
other
Total, other adverse events
0 / 25
serious
Total, serious adverse events
0 / 25

Outcome results

Primary

Collection Using Plerixafor, Etoposide, and Filgrastim

Number of participants able to collect equal to or more than 8 x 10\^6 CD34+ cells/kg with addition of plerixafor to etoposide and filgrastim. These participants are defined as supermobilizers. Participants with less than 8 x 10\^6 CD34+ cells/kg are defined as normal mobilizers.

Time frame: Within 2 days of apheresis

Population: All participants that went on study

ArmMeasureGroupValue (COUNT_OF_PARTICIPANTS)
Treatment (Stem Cell Supermobilization)Collection Using Plerixafor, Etoposide, and FilgrastimNon mobilizers1 Participants
Treatment (Stem Cell Supermobilization)Collection Using Plerixafor, Etoposide, and FilgrastimSupermobilizers7 Participants
Treatment (Stem Cell Supermobilization)Collection Using Plerixafor, Etoposide, and FilgrastimNormal Mobilizers17 Participants
Primary

Overall Survival

Number of participants who receive greater than or equal to 8 x 10\^6 CD34+ cells/kg by 15% following collection with plerixafor, etoposide, and filgrastimstill alive at 1 yr post transplant

Time frame: Up to 1 year post-transplant

Population: Number of supermobilizer participants that were able to achieve collection of ≥ 8 x 106 CD34+ cells/kg

ArmMeasureValue (COUNT_OF_PARTICIPANTS)
Treatment (Stem Cell Supermobilization)Overall Survival7 Participants
Primary

Progression-free Survival

The number of participants of patients who receive greater than or equal to 8 x 10\^6 CD34+ cells/kg following collection with plerixafor, etoposide, and filgrastim and that have progression-free survival at one year

Time frame: Up to 1 year post-transplant

Population: Number of supermobilizer participants that were able to achieve collection of ≥ 8 x 106 CD34+ cells/kg

ArmMeasureValue (COUNT_OF_PARTICIPANTS)
Treatment (Stem Cell Supermobilization)Progression-free Survival7 Participants
Secondary

Correlation of Peripheral CD34+ Cell Count With Graft Content of CD34+ Cells

Correlation of peripheral CD34+ cell count with graft content of CD34+ cells assessed using Spearman correlation.

Time frame: Up to 28 days post treatment

Population: No data collected for this outcome due to low accrual

Secondary

Length of Hospital Stay in Super Mobilizers and Normal Mobilizers

Length of hospital stay in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg.

Time frame: Up to 28 days post treatment

Population: All participants that had some mobilization

ArmMeasureGroupValue (MEAN)Dispersion
Treatment (Stem Cell Supermobilization)Length of Hospital Stay in Super Mobilizers and Normal MobilizersSupermobilizers20.7 daysStandard Deviation 0.5
Treatment (Stem Cell Supermobilization)Length of Hospital Stay in Super Mobilizers and Normal MobilizersNormal Mobilizers22.5 daysStandard Deviation 5.5
Secondary

Need for Remobilization

Number of participants that needed remobilization in supermobilizers and normal mobilizers. Remobilization can be described as follows: The first step for patients undergoing autologous hematopoietic cell transplantation is to mobilize hematopoietic progenitor/stem cells from the bone marrow using G-CSF, plerixafor and/or chemotherapy. This is followed by collection of the cells by apheresis. If sufficient number of progenitor/stem cells cannot be mobilized and then collected by apheresis to proceed with transplantation, it is considered as mobilization failure. For these patients, mobilization of their hematopoietic progenitor/stem cells is attempted a second time (remobilization). The need to do a second 'mobilization' attempt is not ideal.

Time frame: Up to 28 days post treatment

Population: Participants that were mobilized

ArmMeasureGroupValue (COUNT_OF_PARTICIPANTS)
Treatment (Stem Cell Supermobilization)Need for RemobilizationSupermobilizers0 Participants
Treatment (Stem Cell Supermobilization)Need for RemobilizationNormal Mobilizers0 Participants
Secondary

Neutrophil Recovery in Super Mobilizers and Normal Mobilizers

Neutrophil recovery in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg entered as the mean cell count of super mobilizers and normal mobilizers.

Time frame: Up to 28 days post treatment

Population: All participants that had some mobilization

ArmMeasureGroupValue (MEAN)Dispersion
Treatment (Stem Cell Supermobilization)Neutrophil Recovery in Super Mobilizers and Normal MobilizersSupermobilizers10.3 K/ulStandard Deviation 0.5
Treatment (Stem Cell Supermobilization)Neutrophil Recovery in Super Mobilizers and Normal MobilizersNormal Mobilizers10.2 K/ulStandard Deviation 0.7
Secondary

Number of Days of Apheresis Required

Number of days of apheresis required to achieve goal in supermobilizers and normal mobilizers

Time frame: Up to 28 days post treatment

Population: Participants that were mobilized

ArmMeasureGroupValue (MEAN)Dispersion
Treatment (Stem Cell Supermobilization)Number of Days of Apheresis RequiredSupermobilizers1.1 daysStandard Deviation 0.4
Treatment (Stem Cell Supermobilization)Number of Days of Apheresis RequiredNormal Mobilizers2.9 daysStandard Deviation 1.1
Secondary

Number of Transfusion Requirements

Number of transfusions (number of packed red blood cells and platelet transfusions required from day 0 to +28 post-transplant) in supermobilizers and normal mobilizers

Time frame: Up to 28 days post treatment

Population: Participants that were mobilized

ArmMeasureGroupValue (MEAN)Dispersion
Treatment (Stem Cell Supermobilization)Number of Transfusion RequirementsSupermobilizers3.7 transfusionsStandard Deviation 2.1
Treatment (Stem Cell Supermobilization)Number of Transfusion RequirementsNormal Mobilizers4.4 transfusionsStandard Deviation 2
Secondary

Overall Survival in Supermobilizers and Normal Mobilizers

Percentage of participants who were alive 1 year after transplant (OS)

Time frame: Up to 1 year post-transplant

Population: All participants that had some mobilization

ArmMeasureGroupValue (NUMBER)
Treatment (Stem Cell Supermobilization)Overall Survival in Supermobilizers and Normal MobilizersNormal Mobilizers100 percent of participants
Treatment (Stem Cell Supermobilization)Overall Survival in Supermobilizers and Normal MobilizersSupermobilizers100 percent of participants
Secondary

Platelet Recovery in Super Mobilizers and Normal Mobilizers

Platelet recovery in participants receiving greater than or equal to 8 and less than 8 x 10\^6 CD34+ cells/kg.

Time frame: Up to 28 days post treatment

Population: All participants that had some mobilization

ArmMeasureGroupValue (MEAN)Dispersion
Treatment (Stem Cell Supermobilization)Platelet Recovery in Super Mobilizers and Normal MobilizersSupermobilizers20.9 percentage of changeStandard Deviation 6.5
Treatment (Stem Cell Supermobilization)Platelet Recovery in Super Mobilizers and Normal MobilizersNormal Mobilizers19.8 percentage of changeStandard Deviation 5.6
Secondary

Progression-free Survival in Supermobilizers and Normal Mobilizers

Percentage of participants who were alive and free of progression 1 year after transplant (PFS)

Time frame: Up to 1 year post-transplant

Population: All participants that had some mobilization

ArmMeasureGroupValue (NUMBER)
Treatment (Stem Cell Supermobilization)Progression-free Survival in Supermobilizers and Normal MobilizersSupermobilizers100 percent of participants
Treatment (Stem Cell Supermobilization)Progression-free Survival in Supermobilizers and Normal MobilizersNormal Mobilizers82 percent of participants

Source: ClinicalTrials.gov · Data processed: Feb 4, 2026