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Irinotecan in Treating Children With Refractory Solid Tumors

Phase II Trial of Irinotecan in Children With Refractory Solid Tumors

Status
Completed
Phases
Phase 2
Study type
Interventional
Source
ClinicalTrials.gov
Registry ID
NCT00004078
Enrollment
181
Registered
2003-01-28
Start date
1999-10-31
Completion date
Unknown
Last updated
2013-06-14

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Childhood Central Nervous System Germ Cell Tumor, Childhood Choroid Plexus Tumor, Childhood Craniopharyngioma, Childhood Grade III Meningioma, Childhood Grade II Meningioma, Childhood Grade I Meningioma, Childhood Infratentorial Ependymoma, Childhood Oligodendroglioma, Childhood Supratentorial Ependymoma, Previously Treated Childhood Rhabdomyosarcoma, Recurrent Childhood Cerebellar Astrocytoma, Recurrent Childhood Cerebral Astrocytoma, Recurrent Childhood Ependymoma, Recurrent Childhood Medulloblastoma, Recurrent Childhood Rhabdomyosarcoma, Recurrent Childhood Visual Pathway and Hypothalamic Glioma, Recurrent Childhood Visual Pathway Glioma, Recurrent Ewing Sarcoma/Peripheral Primitive Neuroectodermal Tumor, Recurrent Neuroblastoma, Recurrent Osteosarcoma, Unspecified Childhood Solid Tumor, Protocol Specific

Brief summary

This phase II trial is studying irinotecan to see how well it works in treating children with refractory solid tumors. Drugs used in chemotherapy use different ways to stop tumor cells from dividing so they stop growing or die.

Detailed description

OBJECTIVES: I. Determine the efficacy of irinotecan in children with refractory CNS or solid tumors. II. Assess the toxicity, pharmacokinetics, and pharmacodynamics of this regimen in this patient population. III. Determine patient UGT1A1 genotype and correlate genotype with toxicity and pharmacokinetic parameters of this regimen in these patients. OUTLINE: Patients are stratified according to type of solid tumor (Ewings/PNET vs neuroblastoma vs osteosarcoma vs rhabdomyosarcoma vs other solid tumors excluding lymphomas and brain tumors) or brain tumor (medulloblastoma/PNET vs brain stem glioma vs ependymoma vs other CNS tumors). Patients receive irinotecan IV over 60 minutes on days 1-5. Treatment repeats every 3 weeks for at least 2 courses in the absence of disease progression or unacceptable toxicity. Patients are followed every 6 months for 4 years and then annually thereafter until death or until patient enters another POG study.

Interventions

DRUGirinotecan hydrochloride

Given IV

Sponsors

National Cancer Institute (NCI)
CollaboratorNIH
Children's Oncology Group
Lead SponsorNETWORK

Study design

Allocation
NA
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT
Masking
NONE

Eligibility

Sex/Gender
ALL
Age
1 Years to 21 Years
Healthy volunteers
No

Inclusion criteria

* Histologically or cytologically confirmed CNS or solid tumors recurrent or refractory to standard therapy * Solid tumors: * Neuroblastoma * Ewing's Sarcoma/peripheral primitive neuroectodermal tumor (PNET) * Osteosarcoma * Rhabdomyosarcoma * Other extracranial solid tumors * CNS tumors: * Medulloblastoma/PNET * Ependymoma * Brain stem glioma * Other CNS tumor * Intrinsic brain stem tumor (biopsy required only if previously treated with radiosurgery) * Classic optic glioma (histologic requirement waived) * Measurable disease by imaging studies * No lesions assessable only by radionuclide scan * Previously irradiated lesions used to evaluate tumor response must show evidence of an interim increase in size * Performance status - Karnofsky 50-100% if more than 10 years old * Performance status - Lansky 50-100% if 10 years or younger * At least 8 weeks * Absolute neutrophil count greater than 1,000/mm\^3 * Platelet count greater than 100,000/mm\^3 * Hemoglobin greater than 8 mg/dL * Inadequate peripheral blood counts due to bone marrow infiltration allowed * Bilirubin no greater than 1.5 mg/dL * SGPT less than 5 times normal * Creatinine normal * Glomerular filtration rate at least 70 mL/min * No severe uncontrolled infection * Not pregnant or nursing * Negative pregnancy test * Fertile patients must use effective contraception during and for 6 months after study * At least 3 weeks since prior immunotherapy and recovered * No concurrent biologic therapy * At least 3 weeks since prior chemotherapy (8 weeks since prior nitrosoureas) and recovered * No more than 2 prior chemotherapy regimens * No other concurrent chemotherapy * Prior topotecan allowed * No prior irinotecan * Concurrent dexamethasone for brain tumor patients allowed if on a stable or decreasing dose for at least 2 weeks prior to study * At least 3 weeks since prior endocrine therapy * No other concurrent endocrine therapy * See Disease Characteristics * At least 8 weeks since prior extended radiotherapy (including evaluable lesions) and recovered * No prior total body radiotherapy * No concurrent radiotherapy * See Disease Characteristics * At least 3 weeks since prior investigational agents * No other concurrent investigational agents * No concurrent anticonvulsants * No concurrent medications that would interfere with the P-450 enzyme system function (e.g., erythromycin, cimetidine, fluconazole)

Design outcomes

Primary

MeasureTime frame
Objective response (PR or CR), recorded according to standard solid tumor response criteriaUp to 8 years

Secondary

MeasureTime frame
Toxicity, graded using the NCI CTCAE version 2.0Up to 8 years
Pharmacokinetics of irinotecan hydrochlorideDay 1 of course 1

Countries

United States

Outcome results

None listed

Source: ClinicalTrials.gov · Data processed: Feb 4, 2026