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Safety evaluation study for patients with polycythemia vera

Phase I, Open-Label, Multicentre, Dose-Escalation Study to Evaluate the Safety and Pharmacokinetics of A Single Intravenous PPMX-T003 in Polycythemia Vera

Status
Active, not recruiting
Phases
Phase 1
Study type
Interventional
Source
JPRN
Registry ID
JPRN-jRCT2051210083
Enrollment
6
Registered
2021-09-14
Start date
2022-07-27
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Polycythemia Vera Myeloproliferative Neoplasms

Interventions

This drug should be administered within 48 hours after the phlebotomy. In addition, as a dose escalation design, 4 doses of 0.25 mg/kg, 0.4 mg/kg, 0.64 mg/kg, and 1 mg/kg are administered to the same

Sponsors

Ito Tomoki
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: 1. Confirmed diagnosis of PV according to either the 2008 or 2016 WHO classification criteria 2. PV patients being only treated with phlebotomy and the interval is 4-9 weeks

Exclusion criteria

Exclusion criteria: Patients administrated drugs for PV treatment such as hydroxyurea or ruxolitinib (aspirin is excluded)

Design outcomes

Primary

MeasureTime frame
Number of patients Experiencing Treatment-emergent Adverse Events (TEAEs) in the study (vital signs, Evaluation of laboratory test values, Standard 12-lead ECG, physical findings)

Secondary

MeasureTime frame
Pharmacokinetics: Measuring the concentration of PPMX-T003, calculate and assess each PK parameter Immunogenicity: Examining the expression rate and antibody titer of anti-drug antibodies (ADA) Pharmacodynamics: Assessment of the Red blood cell count, hemoglobin, hematocrit, reticulocytes, serum iron, ferritin, total iron binding capacity, transferrin saturation

Contacts

Public ContactTadashi Matsuura

Perseus Proteomics Inc.

tmatsuura@ppmx.com+81-362648268

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026