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Calculation of the Minimal clinically important difference in physical function evaluation for spinal muscular atrophy

Calculation of the Minimal clinically important difference in physical function evaluation for spinal muscular atrophy - Calculation of the Minimal clinically important difference in physical function evaluation for spinal muscular atrophy

Status
Active, not recruiting
Phases
Unknown
Study type
Unknown
Source
JPRN
Registry ID
JPRN-UMIN000054591
Enrollment
30
Registered
2024-06-06
Start date
2024-05-30
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

spinal muscular atrophy

Interventions

None listed

Sponsors

National Center of Neurology and Psychiatry, NCNP
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: Patients who underwent rehabilitation and physical function evaluation at our hospital

Exclusion criteria

Exclusion criteria: Patients for whom functional evaluation could not be performed

Design outcomes

Primary

MeasureTime frame
Hammersmith, Functional Motor Scale Expanded (HFMSE)

Secondary

MeasureTime frame
Grip strength, manual muscle strength test, Revised Upper Limb Module (RULM),

Countries

Japan

Contacts

Public ContactHara Takatoshi

National Center of Neurology and Psychiatry, NCNP Department of Physical Rehabilitation

t_hara1019@ncnp.go.jp042-341-2711

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026