Duchenne muscular dystrophy
Conditions
Interventions
None listed
Sponsors
National Center of Neurology and Psychiatry
Osaka Toneyama Medical Center, Higashisaitama National Hospital, Matsumoto Medical Center, National Hospital Organization Suzuka National Hospital, National Hospital Organization Shimoshizu National Hospital, National Hospital Organization Akita Hospital, National Hospital Organization Hakone National Hospital, National Hospital Organization Nagara Medical Center, Nara Medical University Hospital, Nagano Children'
s Hospital, Nagasaki University Hospital, NHO Iou National Hospital
Eligibility
Sex/Gender
Male
Inclusion criteria
Inclusion criteria: 1. A dystrophin abnormality has been proved by dystrophin genetic test or myopathology, and a definitive diagnosis of DMD has been made. 2. Upper limb motor dysfunction classification at baseline 2007 grade 12 or lower 3. If you are taking steroids, start using them at least 6 months before baseline, and within 3 months, the dosage and administration of steroids will not change and the symptoms will be stable. 4. If you have participated in clinical trials / clinical trials, more than 6 months have passed since the end of study / investigational drug administration at baseline.
Exclusion criteria
Exclusion criteria: 1. The principal investigator or the research coordinator determined that he / she had behavioral abnormalities such as intellectual disability, autistic tendency, and attention deficit hyperactivity disorder that interfered with the implementation of motor function evaluation. 2. Severe heart failure or respiratory failure makes it difficult to visit an outpatient clinic 3. In addition, the principal investigator or the research coordinator judged that it was inappropriate as the subject of this research. 4. Participating in clinical trials / clinical trials at baseline
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| We will perform a multifaceted evaluation of upper limb function obtained from natural history. | — |
Secondary
| Measure | Time frame |
|---|---|
| We will Evaluate ADL, QOL, and swallowing function. | — |
Countries
Japan
Contacts
Public ContactTakatoshi Hara
National Center of Neurology and Psychiatry Department of Rehabilitation Medicine
Outcome results
None listed