Usability Study of Mobile App for Long-Term Follow-Up in Gene Therapy

Usability Study of Mobile App for Long-Term Follow-Up in Gene Therapy - Usability Study of Mobile App for Long-Term Follow-Up in Gene Therapy

Status

Recruiting

Phases

Unknown

Study type

Observational

Source

JPRN

Registry ID

JPRN-UMIN000046480

Enrollment

Registered

2021-12-26

Start date

2021-11-04

Completion date

Unknown

Last updated

2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Patients treated with onasemnogene abeparvovec

Interventions

None listed

Eligibility

Sex/Gender

All

Inclusion criteria

Inclusion criteria: Patients treated with onasemnogene abeparvovec for SMA and the family member over 18 years old

Exclusion criteria

Exclusion criteria: None

Design outcomes

Primary

Measure	Time frame
Survey for the usability of the mobile system	—

Countries

Japan

Contacts

Public ContactMasayoshi Nakakuni

National Center for Child Health and Development Gene and Cell Therapy Promotion Center

nakakuni-m@ncchd.go.jp0334160181

Outcome results