spinal muscular atrophy
Conditions
Interventions
None listed
Sponsors
National Hospital Organization Osaka Toneyama Medical Center
Eligibility
Sex/Gender
All
Inclusion criteria
Inclusion criteria: patient diagnosed as spinal muscular atrophy
Exclusion criteria
Exclusion criteria: patient who is not diagnosed as spinal muscular atrophy
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| General condition, respiratory status, nutritional status, changes in motor function | — |
Secondary
| Measure | Time frame |
|---|---|
| changes in motor function by drug administration | — |
Countries
Japan
Contacts
Public ContactToshio Saito
National Hospital Organization Osaka Toneyama Medical Center Neurology Department
Outcome results
None listed