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Construction of database and analysis of clinical condition of spinal muscular atrophy in NHO Osaka Toneyama Medical Center

Construction of database and analysis of clinical condition of spinal muscular atrophy in NHO Osaka Toneyama Medical Center - Construction of database and analysis of clinical condition of spinal muscular atrophy in NHO Osaka Toneyama Medical Center

Status
Recruiting
Phases
Unknown
Study type
Observational
Source
JPRN
Registry ID
JPRN-UMIN000041696
Enrollment
50
Registered
2020-09-07
Start date
2020-09-07
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

spinal muscular atrophy

Interventions

None listed

Sponsors

National Hospital Organization Osaka Toneyama Medical Center
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: patient diagnosed as spinal muscular atrophy

Exclusion criteria

Exclusion criteria: patient who is not diagnosed as spinal muscular atrophy

Design outcomes

Primary

MeasureTime frame
General condition, respiratory status, nutritional status, changes in motor function

Secondary

MeasureTime frame
changes in motor function by drug administration

Countries

Japan

Contacts

Public ContactToshio Saito

National Hospital Organization Osaka Toneyama Medical Center Neurology Department

saito.toshio.cq@mail.hosp.go.jp06-6853-2001

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026