New Narional Patient Registry for Duchenne muscular dystrophy (Remudy-DMD)

New Narional Patient Registry for Duchenne muscular dystrophy (Remudy-DMD) - Remudy-DMD

Status

Recruiting

Phases

Unknown

Study type

Observational

Source

JPRN

Registry ID

JPRN-UMIN000040768

Enrollment

200

Registered

2020-06-15

Start date

2020-06-15

Completion date

Unknown

Last updated

2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Duchenne muscular dystrophy

Interventions

None listed

Eligibility

Sex/Gender

All

Inclusion criteria

Inclusion criteria: 1. Patients with a dystrophin abnormality proven by dystrophin gene testing or muscle pathology and a definitive diagnosis of DMD 2. Consent form for entry into the registry is available

Exclusion criteria

Exclusion criteria: 1. Consent form for entry into the registry is not available 2. Determined by investigators to be ineligible to participate in this study

Design outcomes

Primary

Measure	Time frame
none	—

Secondary

Measure	Time frame
1. Time to Stand Test (TTSTAND) 2. Time to Run/Walk 10 Meters test (TTRW) 3. Brooke Upper Extremity Scale 4. North Star Ambulatory Assessment (NSAA) 5. Ambulate or not 6. Ventilator use 7. Wheelchair use 8. Cardiac function 9. Respiratory function 10. Medication used 11. QOL 12. Adverse Events	—

Countries

Japan

Contacts

Public ContactTakami Ishizuka

National Center of Neurology and Psychiatry Section of Clinical Research Support, Clinical Research and Education Promotion Division

info-remudy-dmd@ncnp.go.jp042-341-2711

Outcome results