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Modified gross motor function measure for Fukuyama congenital muscular dystrophy

Modified gross motor function measure for Fukuyama congenital muscular dystrophy - Modified GMFM for FCMD

Status
Active, not recruiting
Phases
Unknown
Study type
Interventional
Source
JPRN
Registry ID
JPRN-UMIN000028882
Enrollment
20
Registered
2017-09-01
Start date
2017-09-01
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Fukuyama congenital muscular dystrophy

Interventions

Physical therapists will assess at least once the patients by modified GMFM or GMFM-88

Sponsors

Tokyo Women's Medical University
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: Patients examined at Tokyo Women's Medical University

Exclusion criteria

Exclusion criteria: Patients who receive NPPV or TIV Patients who were thought as inappropriate by us

Design outcomes

Primary

MeasureTime frame
Inter-rater validity

Secondary

MeasureTime frame
Difference of assessment time between by modified GMFM and by GMFM-88

Countries

Japan

Contacts

Public ContactTakatoshi SATO

Tokyo Women's Medical University Department of Pediatrics

takatoshi.sato@twmu.ac.jp03-3353-8111

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026