The prospective cohort study of the enzyme replacement therapy in lysosomal storage disease.

The prospective cohort study of the enzyme replacement therapy in lysosomal storage disease. - Kanagawa Fabry Cohort Study

Status

Recruiting

Phases

Phase 4

Study type

Observational

Source

JPRN

Registry ID

JPRN-UMIN000025321

Enrollment

Registered

2016-12-19

Start date

2012-01-26

Completion date

Unknown

Last updated

2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Lysosomal storage disease

Interventions

None listed

Eligibility

Sex/Gender

All

Inclusion criteria

Inclusion criteria: The lysosomal storage disease patients who need to treat with enzyme replacement therapy.

Exclusion criteria

Exclusion criteria: none

Design outcomes

Primary

Measure	Time frame
QOL( including SF-36)	—

Secondary

Measure	Time frame
renal function state of cerebral lesion heart function	—

Countries

Japan

Contacts

Public ContactNobuhito Hirawa

Yokohama City University Medical Center Department of Hemodialysis and Aphaeresis/ Nephrology and Hypertension

hirawa@yokokohama-cu.ac.jp045-261-5656

Outcome results