A study of the factor related to life-prolongation of patients with Duchenne muscular dystrophy

A study of the factor related to life-prolongation of patients with Duchenne muscular dystrophy - A study of the factor related to life-prolongation of DMD patients

Status

Active, not recruiting

Phases

Unknown

Study type

Observational

Source

JPRN

Registry ID

JPRN-UMIN000016688

Enrollment

300

Registered

2015-03-03

Start date

2015-03-10

Completion date

Unknown

Last updated

2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Duchenne muscular dystrophy

Interventions

None listed

Eligibility

Sex/Gender

Male

Inclusion criteria

Inclusion criteria: Genetically confirmed as Duchenne muscular dystrophy No limitation of disease stage. No limitation of general condition. No limitation of organ function (motor function, respiratory failure, cardiac failure, and dysphagia). Patients with written informed consent. In case of unable to make decision because of the age under 16 years or mental retardation, patient with written informed consent by parents or legal guardian.

Exclusion criteria

Exclusion criteria: Subject meets any of the following criteria is not enrolled in the study. Not confirmed the diagnosis of DMD. Subject considered to be an unsuitable candidate for the study by the Principal investigator or sub-investigator.

Design outcomes

Primary

Measure	Time frame
Time to death	—

Secondary

Measure	Time frame
Time at loss of ambulation	—

Countries

Japan

Contacts

Public ContactToshio Saito

National Hospital Organization Osaka Toneyama Medical Center Clinical research center

saitot@toneyama.go.jp06-6853-2001

Outcome results