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Sirolimus for the treatment of lymphangiomatosis, Gorham-Stout disease and vascular anomalies

Sirolimus for the treatment of lymphangiomatosis, Gorham-Stout disease and vascular anomalies - Sirolimus for vascular anomalies

Status
Active, not recruiting
Phases
Phase 1
Study type
Interventional
Source
JPRN
Registry ID
JPRN-UMIN000016580
Enrollment
30
Registered
2015-02-19
Start date
2015-02-01
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Lymphangiomatosis, Gorham-Stout disease and vascular anomalies

Interventions

Sponsors

Gifu university
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: The patients with intaracbtable lymphangiomatosis, Gorham-Stout disease and vascular anomalies

Exclusion criteria

Exclusion criteria: Allergy of sirolimus

Design outcomes

Primary

MeasureTime frame
Improvement of clinical symptoms at 1, 3, 6, 12 after administration

Countries

Japan

Contacts

Public ContactMichio Ozeki

Gifu University Pediatrics

michioo@gifu-u.ac.jp058-230-6000

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026