FindTrial
Sign In

A gene therapy clinical trial for chronic granulomatous disease targeting the patient's hematopoietic stem cells

A gene therapy clinical trial for chronic granulomatous disease targeting the patient's hematopoietic stem cells - Gene therapy for chronic granulomatous disease

Status
Recruiting
Phases
Phase 1
Study type
Interventional
Source
JPRN
Registry ID
JPRN-UMIN000008235
Enrollment
5
Registered
2012-07-01
Start date
2012-07-01
Completion date
Unknown
Last updated
2026-06-29

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

chronic granulomatous disease

Interventions

infusion of the genetically collected cells

Sponsors

National Center for Child Heath and Development
Lead Sponsor

Eligibility

Sex/Gender
Male

Inclusion criteria

Inclusion criteria: chronic granulomatous disease no choice for stem cell transplantation severe infections

Exclusion criteria

Exclusion criteria: Severe cardiorespiratory failure positive for HIV severe allegy no anticipation for long-term live survival

Design outcomes

Primary

MeasureTime frame
cure or mitigation of severe infections—

Secondary

MeasureTime frame
a long-term protective effect on severe infections—

Countries

Japan

Contacts

Public ContactMASAFUMI ONODOERA

National Center for Child Heath and Development Department of Human Genetics

onodera-m@ncchd.go.jp03-5494-7295

Outcome results

None listed

Source: JPRN (via WHO ICTRP) · Data processed: Jul 3, 2026