familial amyloid polyneuropathy (FAP)
Conditions
Interventions
Sponsors
Shinshu University
Eligibility
Sex/Gender
All
Inclusion criteria
Inclusion criteria: histologically and genetically FAP patients
Exclusion criteria
Exclusion criteria: renal dysfunction pregnancy lactation
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| Clnical FAP scale compound muscle action potential | — |
Secondary
| Measure | Time frame |
|---|---|
| cardiac function mBMI | — |
Countries
Japan
Outcome results
None listed