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Multicenter clinical study of neonatal lysosomal disease

Multicenter clinical study of neonatal lysosomal disease

Status
Active, not recruiting
Phases
Early Phase 1
Study type
Observational
Source
ChiCTR
Registry ID
ChiCTR2100047824
Enrollment
Unknown
Registered
2021-06-27
Start date
2021-07-01
Completion date
Unknown
Last updated
2022-02-28

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Neonatal lysosomal disease

Interventions

Case group:no

Sponsors

The Seventh Medical Center of PLA General Hospital
Lead Sponsor

Eligibility

Sex/Gender
All

Inclusion criteria

Inclusion criteria: 1. Postnatal age <= 28 days; 2. Sign informed consent; 3. Clinical diagnosis and treatment of suspected genetic metabolic diseases.

Exclusion criteria

Exclusion criteria: No.

Design outcomes

Primary

MeasureTime frame
Clinical outcome;Genetic metabolic screening;

Countries

China

Contacts

Public ContactFeng Zhichun

The Seventh Medical Center of PLA General Hospital

Zhjfengzc@126.com+86 10 66721786

Outcome results

None listed

Source: ChiCTR (via WHO ICTRP) · Data processed: Feb 4, 2026