Beta-thalassemia
Conditions
Interventions
Sponsors
Eligibility
Inclusion criteria
Inclusion criteria: 1. Aged 5-18 years; 2. Diagnosis of beta-thalassemia intermedia and major; 3. Guardians have signed the informed consent form; 4. Not participating in other clinical research projects in three months before enrollment; 5. Not taking other drugs such as hydroxyurea that interfered with the therapeutic effect.
Exclusion criteria
Exclusion criteria: 1. Combined with liver, kidney and heart dysfunction; 2. Combined with megaloblastic anemia or other types of anemia; 3. Combined with malignant tumor diseases or rheumatic immunological diseases.
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| Hemoglobin;Transfusion;Hemoglobin composition; | — |
Secondary
| Measure | Time frame |
|---|---|
| Serum ferritin; | — |
Countries
China
Contacts
Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University