immunodeficiency diseases
Conditions
Interventions
Sponsors
Eligibility
Inclusion criteria
Inclusion criteria: Those who meet the clinical manifestations, immune function and genetic diagnostic criteria of immunodeficiency disorders, have severe symptoms and transplantation indications, have suitable donors, and have informed consent.
Exclusion criteria
Exclusion criteria: Contraindication of stem cell transplantation; severe organ damage or failure; unclear genetic diagnosis; other clinical trials such as gene therapy.
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| Engraftment;Immune reconstruction;Survival rate; | — |
Countries
China
Contacts
Children's Hospital of Fudan University