Thalassemia major
Conditions
Interventions
Sponsors
Eligibility
Inclusion criteria
Inclusion criteria: Confirmed diagnosis base on hemotological and genetic criteria; willing and capable to cooperate with scheduled treatment, lab tests/imaging and follow up
Exclusion criteria
Exclusion criteria: non-trasfusion dependent thalassemia; complicated with malignancy; HIV and/or HCV tests positive; incomplete clinical/lab data; status post stem cell transplantation
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| serum ferritin;serum iron;TSH;FT3;FT4;ACTH;cortisol;PTH;serum calcium;Serum phosphate;ALP;25-(OH) Vitamin D;serum glucose;serum insulin;C-Peptide;GHb;HCV Ab;HIV Ab;Temperature;Heart Rate;Repiratory rate;blood pressure;height;Weight;waist/abdominal circumference;Tanner Stage;BMI;Heart, liver and pancreas MRI;CBC; | — |
Secondary
| Measure | Time frame |
|---|---|
| FSH;LH;T;E2; | — |
Countries
China
Contacts
Sun Yat-sen Memorial Hospital, Sun Yat-sen University