Glycogenosis type Ib is an ultra-rare disease, inherited in an autosomal recessive manner.
Conditions
Brief summary
The primary endpoint will be an assessment of the safety and tolerability of empagliflozin, expressed as the type and frequency of adverse reactions throughout the study period. Safety data will be collected at all visits and will be related to possible adverse reactions to empagliflozin as described in the summary of product characteristics.
Detailed description
The secondary objective is to assess efficacy expressed as restoration of neutrophil numbers and function
Interventions
DRUGJardiance 10 mg film-coated tablets
Sponsors
Instytut Pomnik Centrum Zdrowia Dziecka
Eligibility
Sex/Gender
All
Age
0 Years to No maximum
Design outcomes
Primary
| Measure | Time frame |
|---|---|
| The primary endpoint will be an assessment of the safety and tolerability of empagliflozin, expressed as the type and frequency of adverse reactions throughout the study period. Safety data will be collected at all visits and will be related to possible adverse reactions to empagliflozin as described in the summary of product characteristics. | — |
Secondary
| Measure | Time frame |
|---|---|
| The secondary objective is to assess efficacy expressed as restoration of neutrophil numbers and function | — |
Countries
Poland
Outcome results
None listed