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A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of SPR001 (Tildacerfont) in Reducing Supraphysiologic Glucocorticoid Use in Adult Subjects with Classic Congenital Adrenal Hyperplasia

Status
Completed
Phases
Phase 2
Study type
Interventional
Source
EU CTIS
Registry ID
CTIS2023-503771-13-00
Acronym
SPR001-204
Enrollment
44
Registered
2023-04-25
Start date
2021-01-28
Completion date
2024-12-12
Last updated
2024-12-18

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Classic Congenital Adrenal Hyperplasia

Brief summary

Absolute change from baseline in glucocorticoid dose in hydrocortisone equivalent(s) at Week 24

Detailed description

1. 1. Proportion of subjects with baseline GC dose ≤ 35mg HCe who achieve GC dose ≤11 mg/m2/day in HCe and A4 ≤ 1.2x baseline or ≤ ULN at Week 24, 2. Proportion of subjects with GC dose ≤11 mg/m2/day in HCe and A4 ≤ 1.2x baseline or A4 ≤ ULN at Week 24, 3. Proportion of subjects with improvement in at least one cardiovascular risk factor at Week 24.

Interventions

DRUGsame as IMP (Tildacerfont) minus the active substance
DRUGPREDNISOLONE
DRUGPrednisolon 1 mg JENAPHARM®
DRUGHydrocortisone

Sponsors

Spruce Biosciences Inc.
Lead SponsorINDUSTRY

Eligibility

Sex/Gender
All
Age
18 Years to No maximum

Design outcomes

Primary

MeasureTime frame
Absolute change from baseline in glucocorticoid dose in hydrocortisone equivalent(s) at Week 24

Secondary

MeasureTime frame
1. 1. Proportion of subjects with baseline GC dose ≤ 35mg HCe who achieve GC dose ≤11 mg/m2/day in HCe and A4 ≤ 1.2x baseline or ≤ ULN at Week 24, 2. Proportion of subjects with GC dose ≤11 mg/m2/day in HCe and A4 ≤ 1.2x baseline or A4 ≤ ULN at Week 24, 3. Proportion of subjects with improvement in at least one cardiovascular risk factor at Week 24.

Countries

Denmark, Estonia, Germany, Ireland, Italy, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden

Outcome results

None listed

Source: EU CTIS · Data processed: Feb 4, 2026