A Phase 1/2a Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION717 in Patients with Prion Disease

Status

Active, not recruiting

Phases

Phase 1Phase 2

Study type

Interventional

Source

EU CTIS

Registry ID

CTIS2023-503355-98-00

Acronym

ION717-CS2

Enrollment

Registered

2023-10-19

Start date

2024-01-24

Completion date

Unknown

Last updated

2025-09-19

For informational purposes only — not medical advice. Sourced from public registries and may not reflect the latest updates. Terms

Conditions

Prion diseases

None listed

Sex/Gender

All

Age

18 Years to No maximum

France, Germany, Italy, Spain

None listed

Source: EU CTIS · Data processed: Feb 4, 2026