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Vosoritide Injection [Voxzogo]
DRUG
2 trials
Sponsors
University of California, San Francisco
, BioMarin Pharmaceutical
Conditions
Achondroplasia
MPS IVA
MPS VI
Phase 1
Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI
Active, not recruiting
NCT05845749
University of California, San Francisco
MPS IVA, MPS VI
Start: 2023-09-25
End: 2029-12-31
Updated: 2026-03-10
Phase 2
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
Recruiting
NCT07441876
BioMarin Pharmaceutical
Achondroplasia
Start: 2026-04-01
End: 2029-09-01
Target: 160
Updated: 2026-05-07