TransCon CNP
Sponsors
Ascendis Pharma Growth Disorders A/S, Ascendis Pharma A/S, Visen Pharmaceuticals (Shanghai) Co., Ltd.
Conditions
AchondroplasiaAchondroplasia in Children and AdolescentsChildren with Achondroplasia
Phase 2
A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of TransCon CNP Administered Once Weekly in Prepubertal Children With Achondroplasia
CompletedNCT04085523
Start: 2020-06-24End: 2024-10-01Updated: 2026-07-02
A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Multiple Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children With Achondroplasia
CompletedNCT05246033
Start: 2022-01-05End: 2024-04-23Updated: 2026-08-10
AttaCH: A Phase 2, Multicenter, Long-Term, Open Label Extension Trial Evaluating Safety, Tolerability, and Efficacy of Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children and Adolescents with Achondroplasia
RecruitingCTIS2022-502202-33-00
Start: 2023-07-06Target: 113Updated: 2025-11-24
A Clinical Trial to Investigate Long-term Safety, Tolerability, and Efficacy of Weekly Subcutaneous Doses With TransCon CNP in Children and Adolescents With Achondroplasia
Enrolling by invitationNCT05929807
Start: 2023-06-21End: 2039-03-01Target: 140Updated: 2026-08-17
COACH: A Phase 2, Open-Label, Single-Arm, 156-week Trial to Investigate the Efficacy, Safety and Tolerability of Combined Once Weekly Navepegritide and Lonapegsomatropin in Children with Achondroplasia
Active, not recruitingCTIS2023-508341-40-00
Start: 2024-07-26Target: 10Updated: 2025-12-08
teACH: A Phase 2b, Multicenter, Double-Blind, Randomized, Placebo controlled Trial evaluating Efficacy and Safety of Subcutaneous Doses of Navepegritide Administered Once Weekly for 52 Weeks in Adolescents (12-<18 years of age) with Achondroplasia
RecruitingCTIS2024-514208-15-00
Start: 2024-12-10Target: 20Updated: 2025-12-10
ApproaCH: A Phase 2b, Multicenter, Double-Blind, Randomized, Placebo-controlled Trial evaluating Efficacy and Safety of Subcutaneous Doses of TransCon CNP Administered Once Weekly for 52 Weeks in Children with Achondroplasia followed by an Open Label Extension period
CompletedCTIS2024-515469-32-00
Start: 2023-03-02End: 2025-08-13Target: 42Updated: 2025-03-19