Spinraza 12 mg solution for injection

DRUG2 trials

Sponsors

Biogen Idec Research Limited

Conditions

Spinal Muscular Atrophy

Phase 1

An Open Label, Single Cohort Study to Assess the Pharmacokinetic Profile of Nusinersen (BIIB058) Administered via the ThecaFlex DRx™ System (PIERRE-PK)

RecruitingCTIS2024-514239-21-00

Biogen Idec Research LimitedSpinal Muscular Atrophy

Start: 2025-05-21Target: 26Updated: 2026-01-19

Phase 4

A Phase 4 Study of Nusinersen (BIIB058) Among Patients With Spinal Muscular Atrophy Who Received Onasemnogene Abeparvovec - RESPOND

CompletedCTIS2023-505640-18-00

Biogen Idec Research LimitedSpinal Muscular Atrophy

Start: 2021-09-02End: 2025-10-09Target: 25Updated: 2025-10-02