SOBI003

DRUG2 trials

Sponsors

Swedish Orphan Biovitrum

Conditions

Sanfilippo Syndrome Type A (MPS IIIA)

Phase 1

A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients

CompletedNCT03423186

Swedish Orphan BiovitrumSanfilippo Syndrome Type A (MPS IIIA)

Start: 2018-06-19End: 2019-10-25Updated: 2021-11-19

A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients

CompletedNCT03811028

Swedish Orphan BiovitrumSanfilippo Syndrome Type A (MPS IIIA)

Start: 2019-01-19End: 2021-05-07Updated: 2022-02-25

Related Papers

Chemically modified recombinant human sulfamidase (SOBI003) in mucopolysaccharidosis IIIA patients: Results from an open, non-controlled, multicenter study.

2022-06-284 citations