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Skyclarys 50 mg hard capsules
DRUG
3 trials
Sponsors
Reata Pharmaceuticals Inc., Reata Pharmaceuticals Inc.
, Biogen Idec Research Limited
, Fakultni Nemocnice V Motole
Conditions
Friedreich's ataxia
Friedreich’s ataxia
Phase 2
A Phase 2 Study of the Safety, Efficacy, and Pharmacodynamics of RTA 408 in the Treatment of Friedreich's Ataxia (MOXIe)
Completed
CTIS2024-517436-22-00
Reata Pharmaceuticals Inc., Reata Pharmaceuticals Inc.
Friedreich's ataxia
Start: 2016-07-21
End: 2025-06-11
Target: 21
Updated: 2024-12-05
Phase 3
A Phase 3, 2-Part, Randomized, Double-Blind, Placebo-Controlled Study (Part 1) and Open-Label Extension (Part 2) to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Omaveloxolone (BIIB141) in Participants With Friedreich’s Ataxia Aged 2 to < 16 Years
Recruiting
CTIS2025-520896-13-00
Biogen Idec Research Limited
Friedreich’s ataxia
Start: 2025-12-04
Target: 127
Updated: 2025-12-08
Phase 4
Identification of mitochondrial biomarkers reflecting omaveloxolone treatment (in FA patients)
Not yet recruiting
CTIS2025-523881-26-00
Fakultni Nemocnice V Motole
Friedreich's ataxia
Target: 55
Updated: 2026-03-30