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Sepiapterin
DRUG
2 trials
Sponsors
PTC Therapeutics
, Birmingham Women's and Children's NHS Foundation Trust
Conditions
Phenylketonuria
Phase 3
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)
Recruiting
NCT06302348
PTC Therapeutics
Phenylketonuria
Start: 2024-03-04
End: 2031-02-28
Target: 56
Updated: 2026-08-28
Unknown Phase
Impact Of A Phe-Restricted Diet On Gut Health In Children With PKU
Recruiting
NCT07728032
Birmingham Women's and Children's NHS Foundation Trust
Phenylketonuria
Start: 2025-10-01
End: 2026-12-01
Target: 148
Updated: 2026-07-27