SBC-103

DRUG2 trials

Sponsors

Alexion Pharmaceuticals, Inc.

Conditions

Mucopolysaccharidosis III, Type B (MPS IIIB)Mucopolysaccharidosis IIIBSanfilippo B

Phase 1

Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB)

CompletedNCT02324049

Alexion Pharmaceuticals, Inc.Mucopolysaccharidosis IIIB

Start: 2015-01-22End: 2017-10-16Updated: 2018-08-21

A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously

TerminatedNCT02618512

Alexion Pharmaceuticals, Inc.Mucopolysaccharidosis III, Type B (MPS IIIB), Sanfilippo B

Start: 2015-10-15End: 2017-08-18Updated: 2018-04-17