SAF-301

GENETIC2 trials

Sponsors

LYSOGENE

Conditions

Mucopolysaccharidosis Type III ASanfilippo Disease Type A

Phase 1

Intracerebral Gene Therapy for Sanfilippo Type A Syndrome

CompletedNCT01474343

LYSOGENEMucopolysaccharidosis Type III A, Sanfilippo Disease Type A

Start: 2011-08-31End: 2013-05-31Updated: 2014-05-06

Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy

CompletedNCT02053064

LYSOGENEMucopolysaccharidosis Type III A, Sanfilippo Disease Type A

Start: 2013-05-31End: 2017-06-30Updated: 2017-06-20