Skip to content
FindTrial
Search trials
Search trials by condition, treatment, sponsor...
Sign In
Rapamune 2 mg coated tablets
DRUG
2 trials
Sponsors
Centre Hospitalier Universitaire De Toulouse
, Alexion Pharmaceuticals Inc.
Conditions
BAG3 Mutation Associated Dilated Cardiomyopathy
Familial adenomatous polyposis
Phase 1
A Phase 1/2, Open-Label, Dose Finding Study to Investigate the Safety, Tolerability, and Efficacy of ALXN2350 Gene Therapy in Adult Participants with Symptomatic BAG3 Mutation-Associated Dilated Cardiomyopathy
Not yet recruiting
CTIS2024-519674-40-00
Alexion Pharmaceuticals Inc.
BAG3 Mutation Associated Dilated Cardiomyopathy
Target: 8
Updated: 2025-12-12
Phase 2
Safety study for the use of Rapamycin in children with familial adenomatous polyposis - RAPA-4-FAP
Not yet recruiting
CTIS2024-512079-11-00
Centre Hospitalier Universitaire De Toulouse
Familial adenomatous polyposis
Target: 25
Updated: 2025-04-10