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Rapamune 0.5 mg coated tablets

DRUG6 trials

Sponsors

Prevail Therapeutics Inc., Helse Bergen HF, Les Hopitaux Universitaires De Strasbourg, Alexion Pharmaceuticals Inc., Hospital Universitario La Paz

Conditions

BAG3 Mutation Associated Dilated CardiomyopathyFronto-Temporal Dementia with Progranulin Mutations (FTD-GRN)Thyroid eye diseaseType 1 Gaucher Disease (Peripheral/Non-neuronopathic Manifestations)advanced chronic renal insufficiencykidney transplant

Phase 1

Phase 2

Phase 3

Phase 4