Placebo for Mitapivat
Sponsors
Agios Pharmaceuticals Inc.
Conditions
Non–Transfusion-Dependent Alpha- or Beta-ThalassemiaPyruvate Kinase DeficiencyTransfusion-Dependent Alpha- or Beta-Thalassemia
Phase 3
A Phase 3, Double-blind, Randomized, Placebo-Controlled, Multicenter Study Evaluating the Efficacy and Safety of Mitapivat in Subjects With Non–Transfusion-Dependent Alpha or Beta Thalassemia (ENERGIZE)
RecruitingCTIS2024-512745-16-00
Start: 2022-04-13Target: 86Updated: 2026-01-26
A Phase 3, Double-blind, Randomized, Placebo-Controlled, Multicenter Study Evaluating the Efficacy and Safety of Mitapivat in Subjects With Transfusion-Dependent Alpha or Beta Thalassemia (ENERGIZE-T)
Not yet recruitingCTIS2024-512747-23-00
Target: 128Updated: 2026-01-26
A Phase 3, Multicenter, Randomized, Double-blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Subjects With Pyruvate Kinase Deficiency Who Are Regularly Transfused, Followed by a 5-Year Open-label Extension Period
Active, not recruitingCTIS2024-515024-37-00
Start: 2022-05-27Target: 11Updated: 2025-11-19