ORGN001 (formerly ALXN1101)
Sponsors
Origin Biosciences
Conditions
Molybdenum Cofactor Deficiency, Type A
Phase 2
Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP
CompletedNCT02047461
Start: 2014-04-30End: 2022-10-31Updated: 2023-10-17
Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A
CompletedNCT02629393
Start: 2016-05-31End: 2022-10-31Updated: 2023-10-17