Nusinersen Injectable Product
Sponsors
Hospital Israelita Albert Einstein, Newcastle-upon-Tyne Hospitals NHS Trust
Conditions
Spinal Muscular AtrophySpinal Muscular Atrophy (SMA)
Unknown Phase
Characterization of the Clinical-epidemiological Profile of Patients With SMA5q Types II and III: Observational Study
CompletedNCT04404764
Start: 2020-05-27End: 2021-04-23Updated: 2021-04-27
Adult SMA Research and Clinical Hub
RecruitingNCT06978985
Start: 2022-07-29End: 2027-04-30Target: 600Updated: 2025-05-18