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NPC-09
DRUG
2 trials
Sponsors
Tohoku University
, Nobelpharma
Conditions
Distal Myopathy With Rimmed Vacuoles (DMRV)
GNE Myopathy
Hereditary Inclusion Body Myopathy
Hereditary Inclusion Body Myopathy (hIBM)
Nonaka Disease
Nonaka Myopathy
Phase 1
Pharmacokinetic Study on N-acetylneuraminic Acid
Completed
NCT01236898
Tohoku University
Hereditary Inclusion Body Myopathy, Nonaka Myopathy
Start: 2010-11-30
End: 2011-06-30
Updated: 2011-09-08
Phase 3
Efficacy Confirmation Study of NPC-09
Completed
NCT04671472
Nobelpharma
Distal Myopathy With Rimmed Vacuoles (DMRV), GNE Myopathy, Hereditary Inclusion Body Myopathy (hIBM) +1
Start: 2021-02-08
End: 2022-03-29
Updated: 2022-05-16
Related Papers
Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan.
2023-08-11
13 citations