nL-ATN1-002

DRUG2 trials

Sponsors

n-Lorem Foundation

Conditions

Dentatorubral-Pallidoluysian Atrophy

Phase 1

Personalized Antisense Oligonucleotide Therapy for A Single Participant With ATN1 Gene Mutation

Active, not recruitingNCT06706388

n-Lorem FoundationDentatorubral-Pallidoluysian Atrophy

Start: 2024-02-21End: 2027-02-01Updated: 2026-04-09

Personalized Antisense Oligonucleotide for A Single Participant With ATN1 Gene Mutation

Active, not recruitingNCT07084311

n-Lorem FoundationDentatorubral-Pallidoluysian Atrophy

Start: 2024-10-24End: 2026-11-01Updated: 2026-07-13